Mingozzi F - Search Results

1

Enhanced efficacy from gene therapy in Pompe disease using coreceptor blockade.

Han SO, Li S, Brooks ED, Masat E, Leborgne C, Banugaria S, Bird A, Mingozzi F, Waldmann H, Koeberl D. Han SO, et al. Among authors: mingozzi f. Hum Gene Ther. 2015 Jan;26(1):26-35. doi: 10.1089/hum.2014.115. Hum Gene Ther. 2015. PMID: 25382056 Free PMC article.

2

Risk and prevention of anti-factor IX formation in AAV-mediated gene transfer in the context of a large deletion of F9.

Fields PA, Arruda VR, Armstrong E, Chu K, Mingozzi F, Hagstrom JN, Herzog RW, High KA. Fields PA, et al. Among authors: mingozzi f. Mol Ther. 2001 Sep;4(3):201-10. doi: 10.1006/mthe.2001.0441. Mol Ther. 2001. PMID: 11545610 Free article.

3

Therapeutic levels of factor IX expression using a muscle-specific promoter and adeno-associated virus serotype 1 vector.

Liu YL, Mingozzi F, Rodriguéz-Colôn SM, Joseph S, Dobrzynski E, Suzuki T, High KA, Herzog RW. Liu YL, et al. Among authors: mingozzi f. Hum Gene Ther. 2004 Aug;15(8):783-92. doi: 10.1089/1043034041648453. Hum Gene Ther. 2004. PMID: 15319035

4

Major role of local immune responses in antibody formation to factor IX in AAV gene transfer.

Wang L, Cao O, Swalm B, Dobrzynski E, Mingozzi F, Herzog RW. Wang L, et al. Among authors: mingozzi f. Gene Ther. 2005 Oct;12(19):1453-64. doi: 10.1038/sj.gt.3302539. Gene Ther. 2005. PMID: 15889137

5

Muscle as a target for supplementary factor IX gene transfer.

Hoffman BE, Dobrzynski E, Wang L, Hirao L, Mingozzi F, Cao O, Herzog RW. Hoffman BE, et al. Among authors: mingozzi f. Hum Gene Ther. 2007 Jul;18(7):603-13. doi: 10.1089/hum.2007.042. Hum Gene Ther. 2007. PMID: 17594244

6

Undetectable transcription of cap in a clinical AAV vector: implications for preformed capsid in immune responses.

Hauck B, Murphy SL, Smith PH, Qu G, Liu X, Zelenaia O, Mingozzi F, Sommer JM, High KA, Wright JF. Hauck B, et al. Among authors: mingozzi f. Mol Ther. 2009 Jan;17(1):144-52. doi: 10.1038/mt.2008.227. Epub 2008 Oct 21. Mol Ther. 2009. PMID: 18941440 Free PMC article.

7

Proteasome inhibitors decrease AAV2 capsid derived peptide epitope presentation on MHC class I following transduction.

Finn JD, Hui D, Downey HD, Dunn D, Pien GC, Mingozzi F, Zhou S, High KA. Finn JD, et al. Among authors: mingozzi f. Mol Ther. 2010 Jan;18(1):135-42. doi: 10.1038/mt.2009.257. Epub 2009 Nov 10. Mol Ther. 2010. PMID: 19904235 Free PMC article.

8

Correction of pathological accumulation of glycosaminoglycans in central nervous system and peripheral tissues of MPSIIIA mice through systemic AAV9 gene transfer.

Ruzo A, Marcó S, García M, Villacampa P, Ribera A, Ayuso E, Maggioni L, Mingozzi F, Haurigot V, Bosch F. Ruzo A, et al. Among authors: mingozzi f. Hum Gene Ther. 2012 Dec;23(12):1237-46. doi: 10.1089/hum.2012.029. Epub 2012 Oct 17. Hum Gene Ther. 2012. PMID: 22909060

9

Biochemical, histological and functional correction of mucopolysaccharidosis type IIIB by intra-cerebrospinal fluid gene therapy.

Ribera A, Haurigot V, Garcia M, Marcó S, Motas S, Villacampa P, Maggioni L, León X, Molas M, Sánchez V, Muñoz S, Leborgne C, Moll X, Pumarola M, Mingozzi F, Ruberte J, Añor S, Bosch F. Ribera A, et al. Among authors: mingozzi f. Hum Mol Genet. 2015 Apr 1;24(7):2078-95. doi: 10.1093/hmg/ddu727. Epub 2014 Dec 18. Hum Mol Genet. 2015. PMID: 25524704

10

Determination of anti-adeno-associated virus vector neutralizing antibody titer with an in vitro reporter system.

Meliani A, Leborgne C, Triffault S, Jeanson-Leh L, Veron P, Mingozzi F. Meliani A, et al. Among authors: mingozzi f. Hum Gene Ther Methods. 2015 Apr;26(2):45-53. doi: 10.1089/hgtb.2015.037. Hum Gene Ther Methods. 2015. PMID: 25819687 Free PMC article.

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