Non-Ambulant Duchenne Patients Theoretically Treatable by Exon 53 Skipping have Severe Phenotype.
Servais L, Montus M, Guiner CL, Ben Yaou R, Annoussamy M, Moraux A, Hogrel JY, Seferian AM, Zehrouni K, Le Moing AG, Gidaro T, Vanhulle C, Laugel V, Butoianu N, Cuisset JM, Sabouraud P, Cances C, Klein A, Leturcq F, Moullier P, Voit T.
Servais L, et al. Among authors: gidaro t.
J Neuromuscul Dis. 2015 Sep 2;2(3):269-279. doi: 10.3233/JND-150100.
J Neuromuscul Dis. 2015.
PMID: 27858743
Free PMC article.