Koeberl D - Search Results

1

Synergistic Efficacy from Gene Therapy with Coreceptor Blockade and a β2-Agonist in Murine Pompe Disease.

Han SO, Li S, Bird A, Koeberl D. Han SO, et al. Among authors: koeberl d. Hum Gene Ther. 2015 Nov;26(11):743-50. doi: 10.1089/hum.2015.033. Epub 2015 Sep 29. Hum Gene Ther. 2015. PMID: 26417913 Free PMC article.

2

Delivery of glucose-6-phosphatase in a canine model for glycogen storage disease, type Ia, with adeno-associated virus (AAV) vectors.

Beaty RM, Jackson M, Peterson D, Bird A, Brown T, Benjamin DK Jr, Juopperi T, Kishnani P, Boney A, Chen YT, Koeberl DD. Beaty RM, et al. Among authors: koeberl dd. Gene Ther. 2002 Aug;9(15):1015-22. doi: 10.1038/sj.gt.3301728. Gene Ther. 2002. PMID: 12101432

3

Long-term correction of glycogen storage disease type II with a hybrid Ad-AAV vector.

Sun BD, Chen YT, Bird A, Amalfitano A, Koeberl DD. Sun BD, et al. Among authors: koeberl dd. Mol Ther. 2003 Feb;7(2):193-201. doi: 10.1016/s1525-0016(02)00055-2. Mol Ther. 2003. PMID: 12597907 Free article.

4

Packaging of an AAV vector encoding human acid alpha-glucosidase for gene therapy in glycogen storage disease type II with a modified hybrid adenovirus-AAV vector.

Sun B, Chen YT, Bird A, Xu F, Hou YX, Amalfitano A, Koeberl DD. Sun B, et al. Among authors: koeberl dd. Mol Ther. 2003 Apr;7(4):467-77. doi: 10.1016/s1525-0016(03)00022-4. Mol Ther. 2003. PMID: 12727109 Free article.

5

Efficacy of an adeno-associated virus 8-pseudotyped vector in glycogen storage disease type II.

Sun B, Zhang H, Franco LM, Young SP, Schneider A, Bird A, Amalfitano A, Chen YT, Koeberl DD. Sun B, et al. Among authors: koeberl dd. Mol Ther. 2005 Jan;11(1):57-65. doi: 10.1016/j.ymthe.2004.10.004. Mol Ther. 2005. PMID: 15585406 Free article.

6

Correction of glycogen storage disease type II by an adeno-associated virus vector containing a muscle-specific promoter.

Sun B, Zhang H, Franco LM, Brown T, Bird A, Schneider A, Koeberl DD. Sun B, et al. Among authors: koeberl dd. Mol Ther. 2005 Jun;11(6):889-98. doi: 10.1016/j.ymthe.2005.01.012. Mol Ther. 2005. PMID: 15922959 Free article.

7

Evasion of immune responses to introduced human acid alpha-glucosidase by liver-restricted expression in glycogen storage disease type II.

Franco LM, Sun B, Yang X, Bird A, Zhang H, Schneider A, Brown T, Young SP, Clay TM, Amalfitano A, Chen YT, Koeberl DD. Franco LM, et al. Among authors: koeberl dd. Mol Ther. 2005 Nov;12(5):876-84. doi: 10.1016/j.ymthe.2005.04.024. Epub 2005 Jul 6. Mol Ther. 2005. PMID: 16005263 Free article.

8

Complete correction of hyperphenylalaninemia following liver-directed, recombinant AAV2/8 vector-mediated gene therapy in murine phenylketonuria.

Harding CO, Gillingham MB, Hamman K, Clark H, Goebel-Daghighi E, Bird A, Koeberl DD. Harding CO, et al. Among authors: koeberl dd. Gene Ther. 2006 Mar;13(5):457-62. doi: 10.1038/sj.gt.3302678. Gene Ther. 2006. PMID: 16319949 Free PMC article.

9

Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia.

Koeberl DD, Sun BD, Damodaran TV, Brown T, Millington DS, Benjamin DK Jr, Bird A, Schneider A, Hillman S, Jackson M, Beaty RM, Chen YT. Koeberl DD, et al. Gene Ther. 2006 Sep;13(17):1281-9. doi: 10.1038/sj.gt.3302774. Epub 2006 May 4. Gene Ther. 2006. PMID: 16672983

10

Enhanced efficacy of an AAV vector encoding chimeric, highly secreted acid alpha-glucosidase in glycogen storage disease type II.

Sun B, Zhang H, Benjamin DK Jr, Brown T, Bird A, Young SP, McVie-Wylie A, Chen YT, Koeberl DD. Sun B, et al. Among authors: koeberl dd. Mol Ther. 2006 Dec;14(6):822-30. doi: 10.1016/j.ymthe.2006.08.001. Epub 2006 Sep 20. Mol Ther. 2006. PMID: 16987711 Free PMC article.

Save citations to file

Email citations

Send citations to clipboard

Add to Collections

Add to My Bibliography

Create a file for external citation management software

Your saved search

Your RSS Feed

My Custom Filters

Publication date

Text availability

Article attribute

Article type

Article Language

Species

Sex

Age

Other

151 results

Search Page

Filters