A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies.
Wilk J, Aggarwal V, Pauley M, Corey D, Conrado DJ, Lingineni K, Morales JF, Yoon DY, Zhang Y, Cui Z, Burton J, Larkindale J, Ma SC, Hovinga C, Martinez T, Romero K, Belfiore-Oshan R, Kim S; Duchenne Regulatory Science Consortium (D‐RSC) and the CINRG DNHS investigators.
Wilk J, et al. Among authors: ma sc.
CPT Pharmacometrics Syst Pharmacol. 2024 Nov 27. doi: 10.1002/psp4.13281. Online ahead of print.
CPT Pharmacometrics Syst Pharmacol. 2024.
PMID: 39600251