ML372 blocks SMN ubiquitination and improves spinal muscular atrophy pathology in mice.
Abera MB, Xiao J, Nofziger J, Titus S, Southall N, Zheng W, Moritz KE, Ferrer M, Cherry JJ, Androphy EJ, Wang A, Xu X, Austin C, Fischbeck KH, Marugan JJ, Burnett BG.
Abera MB, et al. Among authors: burnett bg.
JCI Insight. 2016 Nov 17;1(19):e88427. doi: 10.1172/jci.insight.88427.
JCI Insight. 2016.
PMID: 27882347
Free PMC article.