Lentivirus-mediated gene therapy for Fabry disease.
Khan A, Barber DL, Huang J, Rupar CA, Rip JW, Auray-Blais C, Boutin M, O'Hoski P, Gargulak K, McKillop WM, Fraser G, Wasim S, LeMoine K, Jelinski S, Chaudhry A, Prokopishyn N, Morel CF, Couban S, Duggan PR, Fowler DH, Keating A, West ML, Foley R, Medin JA.
Khan A, et al. Among authors: barber dl.
Nat Commun. 2021 Feb 25;12(1):1178. doi: 10.1038/s41467-021-21371-5.
Nat Commun. 2021.
PMID: 33633114
Free PMC article.
Clinical Trial.