Cherqui S - Search Results

1

Transplantation of wild-type mouse hematopoietic stem and progenitor cells ameliorates deficits in a mouse model of Friedreich's ataxia.

Rocca CJ, Goodman SM, Dulin JN, Haquang JH, Gertsman I, Blondelle J, Smith JLM, Heyser CJ, Cherqui S. Rocca CJ, et al. Among authors: cherqui s. Sci Transl Med. 2017 Oct 25;9(413):eaaj2347. doi: 10.1126/scitranslmed.aaj2347. Sci Transl Med. 2017. PMID: 29070698 Free PMC article.

2

Successful treatment of the murine model of cystinosis using bone marrow cell transplantation.

Syres K, Harrison F, Tadlock M, Jester JV, Simpson J, Roy S, Salomon DR, Cherqui S. Syres K, et al. Among authors: cherqui s. Blood. 2009 Sep 17;114(12):2542-52. doi: 10.1182/blood-2009-03-213934. Epub 2009 Jun 8. Blood. 2009. PMID: 19506297 Free article.

3

Hematopoietic stem cell gene therapy for the multisystemic lysosomal storage disorder cystinosis.

Harrison F, Yeagy BA, Rocca CJ, Kohn DB, Salomon DR, Cherqui S. Harrison F, et al. Among authors: cherqui s. Mol Ther. 2013 Feb;21(2):433-44. doi: 10.1038/mt.2012.214. Epub 2012 Oct 23. Mol Ther. 2013. PMID: 23089735 Free PMC article.

4

Upregulation of the Rab27a-dependent trafficking and secretory mechanisms improves lysosomal transport, alleviates endoplasmic reticulum stress, and reduces lysosome overload in cystinosis.

Johnson JL, Napolitano G, Monfregola J, Rocca CJ, Cherqui S, Catz SD. Johnson JL, et al. Among authors: cherqui s. Mol Cell Biol. 2013 Aug;33(15):2950-62. doi: 10.1128/MCB.00417-13. Epub 2013 May 28. Mol Cell Biol. 2013. PMID: 23716592 Free PMC article.

5

rAAV9 combined with renal vein injection is optimal for kidney-targeted gene delivery: conclusion of a comparative study.

Rocca CJ, Ur SN, Harrison F, Cherqui S. Rocca CJ, et al. Among authors: cherqui s. Gene Ther. 2014 Jun;21(6):618-28. doi: 10.1038/gt.2014.35. Epub 2014 May 1. Gene Ther. 2014. PMID: 24784447 Free PMC article.

6

Brief reports: Lysosomal cross-correction by hematopoietic stem cell-derived macrophages via tunneling nanotubes.

Naphade S, Sharma J, Gaide Chevronnay HP, Shook MA, Yeagy BA, Rocca CJ, Ur SN, Lau AJ, Courtoy PJ, Cherqui S. Naphade S, et al. Among authors: cherqui s. Stem Cells. 2015 Jan;33(1):301-9. doi: 10.1002/stem.1835. Stem Cells. 2015. PMID: 25186209 Free PMC article.

7

Impairment of chaperone-mediated autophagy leads to selective lysosomal degradation defects in the lysosomal storage disease cystinosis.

Napolitano G, Johnson JL, He J, Rocca CJ, Monfregola J, Pestonjamasp K, Cherqui S, Catz SD. Napolitano G, et al. Among authors: cherqui s. EMBO Mol Med. 2015 Feb;7(2):158-74. doi: 10.15252/emmm.201404223. EMBO Mol Med. 2015. PMID: 25586965 Free PMC article.

8

Treatment of Inherited Eye Defects by Systemic Hematopoietic Stem Cell Transplantation.

Rocca CJ, Kreymerman A, Ur SN, Frizzi KE, Naphade S, Lau A, Tran T, Calcutt NA, Goldberg JL, Cherqui S. Rocca CJ, et al. Among authors: cherqui s. Invest Ophthalmol Vis Sci. 2015 Nov;56(12):7214-23. doi: 10.1167/iovs.15-17107. Invest Ophthalmol Vis Sci. 2015. PMID: 26540660 Free PMC article.

9

Hematopoietic Stem Cells Transplantation Can Normalize Thyroid Function in a Cystinosis Mouse Model.

Gaide Chevronnay HP, Janssens V, Van Der Smissen P, Rocca CJ, Liao XH, Refetoff S, Pierreux CE, Cherqui S, Courtoy PJ. Gaide Chevronnay HP, et al. Among authors: cherqui s. Endocrinology. 2016 Apr;157(4):1363-71. doi: 10.1210/en.2015-1762. Epub 2016 Jan 26. Endocrinology. 2016. PMID: 26812160 Free PMC article.

10

Cystinosin, the small GTPase Rab11, and the Rab7 effector RILP regulate intracellular trafficking of the chaperone-mediated autophagy receptor LAMP2A.

Zhang J, Johnson JL, He J, Napolitano G, Ramadass M, Rocca C, Kiosses WB, Bucci C, Xin Q, Gavathiotis E, Cuervo AM, Cherqui S, Catz SD. Zhang J, et al. Among authors: cherqui s. J Biol Chem. 2017 Jun 23;292(25):10328-10346. doi: 10.1074/jbc.M116.764076. Epub 2017 May 2. J Biol Chem. 2017. PMID: 28465352 Free PMC article.

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