ASO targeting RBM3 temperature-controlled poison exon splicing prevents neurodegeneration in vivo.
Preußner M, Smith HL, Hughes D, Zhang M, Emmerichs AK, Scalzitti S, Peretti D, Swinden D, Neumann A, Haltenhof T, Mallucci GR, Heyd F.
Preußner M, et al. Among authors: mallucci gr.
EMBO Mol Med. 2023 May 8;15(5):e17157. doi: 10.15252/emmm.202217157. Epub 2023 Mar 22.
EMBO Mol Med. 2023.
PMID: 36946385
Free PMC article.