Natural gene therapy by reverse mosaicism leads to improved hematology in Fanconi anemia patients.
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Ramírez MJ, et al. Among authors: nicoletti e.
Am J Hematol. 2021 Aug 1;96(8):989-999. doi: 10.1002/ajh.26234. Epub 2021 May 25.
Am J Hematol. 2021.
PMID: 33984160
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