Nonconditioned ADA-SCID gene therapy reveals ADA requirement in the hematopoietic system and clonal dominance of vector-marked clones.
Uchiyama T, Takahashi S, Nakabayashi K, Okamura K, Edasawa K, Yamada M, Watanabe N, Mochizuki E, Yasuda T, Miura A, Kato M, Tomizawa D, Otsu M, Ariga T, Onodera M.
Uchiyama T, et al. Among authors: okamura k.
Mol Ther Methods Clin Dev. 2021 Oct 16;23:424-433. doi: 10.1016/j.omtm.2021.10.003. eCollection 2021 Dec 10.
Mol Ther Methods Clin Dev. 2021.
PMID: 34786435
Free PMC article.