Clinical spectrum of POLR3-related leukodystrophy caused by biallelic POLR1C pathogenic variants.
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Neurol Genet. 2019 Oct 30;5(6):e369. doi: 10.1212/NXG.0000000000000369. eCollection 2019 Dec.
Neurol Genet. 2019.
PMID: 32042905
Free PMC article.