Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation

Search Page

Filters

My Custom Filters

Publication date

Text availability

Article attribute

Article type

Additional filters

Article Language

Species

Sex

Age

Other

Search Results

5 results

Filters applied: . Clear all
Results are displayed in a computed author sort order. The Publication Date timeline is not available.
Page 1
What's new and what's next for gene therapy in Pompe disease?
Roger AL, Sethi R, Huston ML, Scarrow E, Bao-Dai J, Lai E, Biswas DD, El Haddad L, Strickland LM, Kishnani PS, ElMallah MK. Roger AL, et al. Expert Opin Biol Ther. 2022 Sep;22(9):1117-1135. doi: 10.1080/14712598.2022.2067476. Epub 2022 Apr 27. Expert Opin Biol Ther. 2022. PMID: 35428407 Free PMC article.
Breathing in Duchenne muscular dystrophy: translation to therapy.
Mhandire DZ, Burns DP, Roger AL, O'Halloran KD, ElMallah MK. Mhandire DZ, et al. Among authors: roger al. J Physiol. 2022 Aug;600(15):3465-3482. doi: 10.1113/JP281671. Epub 2022 Jun 24. J Physiol. 2022. PMID: 35620971 Free PMC article. Review.
GAA deficiency disrupts distal airway cells in Pompe disease.
El Haddad L, Lai E, Murthy PKL, Biswas DD, Soufny R, Roger AL, Tata PR, ElMallah MK. El Haddad L, et al. Among authors: roger al. Am J Physiol Lung Cell Mol Physiol. 2023 Sep 1;325(3):L288-L298. doi: 10.1152/ajplung.00032.2023. Epub 2023 Jun 27. Am J Physiol Lung Cell Mol Physiol. 2023. PMID: 37366541 Free PMC article.