North Star Ambulatory Assessment changes in ambulant Duchenne boys amenable to skip exons 44, 45, 51, and 53: A 3 year follow up.
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Coratti G, et al. Among authors: de groot i, de lucia s.
PLoS One. 2021 Jun 25;16(6):e0253882. doi: 10.1371/journal.pone.0253882. eCollection 2021.
PLoS One. 2021.
PMID: 34170974
Free PMC article.