Dysfunction of proprioceptive sensory synapses is a pathogenic event and therapeutic target in mice and humans with spinal muscular atrophy.
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medRxiv [Preprint]. 2024 Jun 4:2024.06.03.24308132. doi: 10.1101/2024.06.03.24308132.
medRxiv. 2024.
PMID: 38883729
Free PMC article.
Preprint.