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Page 1
Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A.
Mahlangu J, Kaczmarek R, von Drygalski A, Shapiro S, Chou SC, Ozelo MC, Kenet G, Peyvandi F, Wang M, Madan B, Key NS, Laffan M, Dunn AL, Mason J, Quon DV, Symington E, Leavitt AD, Oldenburg J, Chambost H, Reding MT, Jayaram K, Yu H, Mahajan R, Chavele KM, Reddy DB, Henshaw J, Robinson TM, Wong WY, Pipe SW; GENEr8-1 Trial Group. Mahlangu J, et al. Among authors: henshaw j. N Engl J Med. 2023 Feb 23;388(8):694-705. doi: 10.1056/NEJMoa2211075. N Engl J Med. 2023. PMID: 36812433 Clinical Trial.
Clinical immunogenicity outcomes from GENEr8-1, a phase 3 study of valoctocogene roxaparvovec, an AAV5-vectored gene therapy for hemophilia A.
Long BR, Robinson TM, Day JRS, Yu H, Lau K, Imtiaz U, Patton KS, de Hart G, Henshaw J, Agarwal S, Vettermann C, Zoog SJ, Gupta S. Long BR, et al. Among authors: henshaw j. Mol Ther. 2024 Jul 3;32(7):2052-2063. doi: 10.1016/j.ymthe.2024.05.033. Epub 2024 May 24. Mol Ther. 2024. PMID: 38796703 Free article. Clinical Trial.
Development of a Weight-Band Dosing Approach for Vosoritide in Children with Achondroplasia Using a Population Pharmacokinetic Model.
Qi Y, Chan ML, Mould DR, Larimore K, Fisheleva E, Cherukuri A, Day J, Savarirayan R, Irving M, Bacino CA, Hoover-Fong J, Ozono K, Mohnike K, Wilcox WR, Bober MB, Henshaw J. Qi Y, et al. Among authors: henshaw j. Clin Pharmacokinet. 2024 May;63(5):707-719. doi: 10.1007/s40262-024-01371-6. Epub 2024 Apr 23. Clin Pharmacokinet. 2024. PMID: 38649657 Free PMC article.
Safety, pharmacokinetics and CNS distribution of tralesinidase alfa administered via intracerebroventricular infusion to juvenile cynomolgus monkeys.
Pinkstaff J, McCullagh E, Grover A, Melton AC, Cherukuri A, Wait JC, Nguyen A, Butt MT, Trombley JL, Reed RP, Adams EL, Boyd RB, Chandra S, Henshaw J, O'Neill CA, Zanelli E, Kovalchin J. Pinkstaff J, et al. Among authors: henshaw j. Toxicol Rep. 2023 Mar 1;10:357-366. doi: 10.1016/j.toxrep.2023.02.014. eCollection 2023. Toxicol Rep. 2023. PMID: 36923444 Free PMC article.
Search for Leptonic Decays of Dark Photons at NA62.
Cortina Gil E, Jerhot J, Kleimenova A, Lurkin N, Zamkovsky M, Numao T, Velghe B, Wong VWS, Bryman D, Hives Z, Husek T, Kampf K, Koval M, De Martino B, Perrin-Terrin M, Döbrich B, Lezki S, Akmete AT, Aliberti R, Di Lella L, Doble N, Peruzzo L, Schuchmann S, Wahl H, Wanke R, Dalpiaz P, Neri I, Petrucci F, Soldani M, Bandiera L, Cotta Ramusino A, Gianoli A, Romagnoni M, Sytov A, Lenti M, Lo Chiatto P, Marchevski R, Panichi I, Ruggiero G, Bizzeti A, Bucci F, Antonelli A, Kozhuharov V, Lanfranchi G, Martellotti S, Moulson M, Spadaro T, Tinti G, Ambrosino F, D'Errico M, Fiorenza R, Giordano R, Massarotti P, Mirra M, Napolitano M, Rosa I, Saracino G, Anzivino G, Brizioli F, Cenci P, Duk V, Lollini R, Lubrano P, Pepe M, Piccini M, Costantini F, Giorgi M, Giudici S, Lamanna G, Lari E, Pedreschi E, Pinzino J, Sozzi M, Fantechi R, Spinella F, Mannelli I, Raggi M, Biagioni A, Cretaro P, Frezza O, Lonardo A, Turisini M, Vicini P, Ammendola R, Bonaiuto V, Fucci A, Salamon A, Sargeni F, Arcidiacono R, Bloch-Devaux B, Menichetti E, Migliore E, Biino C, Filippi A, Marchetto F, Soldi D, Briano Olvera A, Engelfried J, Estrada-Tristan N, Piandani R, Reyes Santos MA, Rodriguez Rivera KA, Boboc P, Brag… See abstract for full author list ➔ Cortina Gil E, et al. Among authors: henshaw j. Phys Rev Lett. 2024 Sep 13;133(11):111802. doi: 10.1103/PhysRevLett.133.111802. Phys Rev Lett. 2024. PMID: 39331997
125 results