Base-edited cynomolgus monkeys mimic core symptoms of STXBP1 encephalopathy.
Lu Z, He S, Jiang J, Zhuang L, Wang Y, Yang G, Jiang X, Nie Y, Fu J, Zhang X, Lu Y, Bian X, Chang HC, Xiong Z, Huang X, Liu Z, Sun Q.
Lu Z, et al. Among authors: sun q.
Mol Ther. 2022 Jun 1;30(6):2163-2175. doi: 10.1016/j.ymthe.2022.03.001. Epub 2022 Mar 11.
Mol Ther. 2022.
PMID: 35283272
Free PMC article.