Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation

Search Page

Filters

My Custom Filters

Publication date

Text availability

Article attribute

Article type

Additional filters

Article Language

Species

Sex

Age

Other

Search Results

360 results

Filters applied: . Clear all
Results are displayed in a computed author sort order. The Publication Date timeline is not available.
Page 1
Gene therapy for blood diseases.
Kohn DB. Kohn DB. Curr Opin Biotechnol. 2019 Dec;60:39-45. doi: 10.1016/j.copbio.2018.11.016. Epub 2018 Dec 29. Curr Opin Biotechnol. 2019. PMID: 30599357 Review.
Improved Titer and Gene Transfer by Lentiviral Vectors Using Novel, Small β-Globin Locus Control Region Elements.
Morgan RA, Unti MJ, Aleshe B, Brown D, Osborne KS, Koziol C, Ayoub PG, Smith OB, O'Brien R, Tam C, Miyahira E, Ruiz M, Quintos JP, Senadheera S, Hollis RP, Kohn DB. Morgan RA, et al. Among authors: kohn db. Mol Ther. 2020 Jan 8;28(1):328-340. doi: 10.1016/j.ymthe.2019.09.020. Epub 2019 Sep 28. Mol Ther. 2020. PMID: 31628051 Free PMC article.
Creating New β-Globin-Expressing Lentiviral Vectors by High-Resolution Mapping of Locus Control Region Enhancer Sequences.
Morgan RA, Ma F, Unti MJ, Brown D, Ayoub PG, Tam C, Lathrop L, Aleshe B, Kurita R, Nakamura Y, Senadheera S, Wong RL, Hollis RP, Pellegrini M, Kohn DB. Morgan RA, et al. Among authors: kohn db. Mol Ther Methods Clin Dev. 2020 Apr 18;17:999-1013. doi: 10.1016/j.omtm.2020.04.006. eCollection 2020 Jun 12. Mol Ther Methods Clin Dev. 2020. PMID: 32426415 Free PMC article.
Global and Local Manipulation of DNA Repair Mechanisms to Alter Site-Specific Gene Editing Outcomes in Hematopoietic Stem Cells.
Benitez EK, Lomova Kaufman A, Cervantes L, Clark DN, Ayoub PG, Senadheera S, Osborne K, Sanchez JM, Crisostomo RV, Wang X, Reuven N, Shaul Y, Hollis RP, Romero Z, Kohn DB. Benitez EK, et al. Among authors: kohn db. Front Genome Ed. 2020 Dec 10;2:601541. doi: 10.3389/fgeed.2020.601541. eCollection 2020. Front Genome Ed. 2020. PMID: 34713224 Free PMC article.
Outcomes following treatment for ADA-deficient severe combined immunodeficiency: a report from the PIDTC.
Cuvelier GDE, Logan BR, Prockop SE, Buckley RH, Kuo CY, Griffith LM, Liu X, Yip A, Hershfield MS, Ayoub PG, Moore TB, Dorsey MJ, O'Reilly RJ, Kapoor N, Pai SY, Kapadia M, Ebens CL, Forbes Satter LR, Burroughs LM, Petrovic A, Chellapandian D, Heimall J, Shyr DC, Rayes A, Bednarski JJ, Chandra S, Chandrakasan S, Gillio AP, Madden L, Quigg TC, Caywood EH, Dávila Saldaña BJ, DeSantes K, Eissa H, Goldman FD, Rozmus J, Shah AJ, Vander Lugt MT, Thakar MS, Parrott RE, Martinez C, Leiding JW, Torgerson TR, Pulsipher MA, Notarangelo LD, Cowan MJ, Dvorak CC, Haddad E, Puck JM, Kohn DB. Cuvelier GDE, et al. Among authors: kohn db. Blood. 2022 Aug 18;140(7):685-705. doi: 10.1182/blood.2022016196. Blood. 2022. PMID: 35671392 Free PMC article. Clinical Trial.
Diverse Approaches to Gene Therapy of Sickle Cell Disease.
White SL, Hart K, Kohn DB. White SL, et al. Among authors: kohn db. Annu Rev Med. 2023 Jan 27;74:473-487. doi: 10.1146/annurev-med-042921-021707. Epub 2022 Sep 6. Annu Rev Med. 2023. PMID: 36067800 Free PMC article. Review.
β-Thalassemia: all about that base, no cutting.
Ayoub PG, Kohn DB. Ayoub PG, et al. Among authors: kohn db. Blood. 2023 Mar 9;141(10):1098-1099. doi: 10.1182/blood.2022019350. Blood. 2023. PMID: 36893006 Free article. No abstract available.
Successes and challenges in clinical gene therapy.
Kohn DB, Chen YY, Spencer MJ. Kohn DB, et al. Gene Ther. 2023 Nov;30(10-11):738-746. doi: 10.1038/s41434-023-00390-5. Epub 2023 Nov 8. Gene Ther. 2023. PMID: 37935854 Free PMC article.
360 results