Targeting neuronal lysosomal dysfunction caused by β-glucocerebrosidase deficiency with an enzyme-based brain shuttle construct.
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Nat Commun. 2023 Apr 12;14(1):2057. doi: 10.1038/s41467-023-37632-4.
Nat Commun. 2023.
PMID: 37045813
Free PMC article.