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Page 1
Quantifying and mitigating motor phenotypes induced by antisense oligonucleotides in the central nervous system.
Moazami MP, Rembetsy-Brown JM, Sarli SL, McEachern HR, Wang F, Ohara M, Wagh A, Kelly K, Krishnamurthy PM, Weiss A, Marosfoi M, King RM, Motwani M, Gray-Edwards H, Fitzgerald KA, Brown RH, Watts JK. Moazami MP, et al. Among authors: gray edwards h. Mol Ther. 2024 Oct 28:S1525-0016(24)00684-1. doi: 10.1016/j.ymthe.2024.10.024. Online ahead of print. Mol Ther. 2024. PMID: 39460376 Free article.
Quantitative reliability assessment of brain MRI volumetric measurements in type II GM1 gangliosidosis patients.
Zoppo C, Kolstad J, Johnston J, D'Souza P, Kühn AL, Vardar Z, Peker A, Lindsay C, Rentiya ZS, King R, Gray-Edwards H, Vachha B, Acosta MT, Tifft CJ, Shazeeb MS. Zoppo C, et al. Among authors: gray edwards h. Front Neuroimaging. 2024 Sep 13;3:1410848. doi: 10.3389/fnimg.2024.1410848. eCollection 2024. Front Neuroimaging. 2024. PMID: 39350771 Free PMC article.
A minimally invasive endovascular approach to the cerebellopontine angle cistern enables broad CNS biodistribution of scAAV9-CB-GFP.
Benatti HR, Anagnostakou V, Taghian T, Hall EF, Nath S, Heilman CB, Beneduce BM, Leporati A, Raskett C, Epshtein M, King R, Gounis MJ, Malek AM, Gray-Edwards HL. Benatti HR, et al. Among authors: gray edwards hl. Mol Ther. 2024 Oct 2;32(10):3346-3355. doi: 10.1016/j.ymthe.2024.08.024. Epub 2024 Aug 26. Mol Ther. 2024. PMID: 39192584 Free PMC article.
Awake intracerebroventricular delivery and safety assessment of oligonucleotides in a large animal model.
Benatti HR, Prestigiacomo RD, Taghian T, Miller R, King R, Gounis MJ, Celik U, Bertrand S, Tuominen S, Bierfeldt L, Parsley E, Gallagher J, Hall EF, McElroy AW, Sena-Esteves M, Khvorova A, Aronin N, Gray-Edwards HL. Benatti HR, et al. Among authors: gray edwards hl. Mol Ther Methods Clin Dev. 2023 Sep 26;31:101122. doi: 10.1016/j.omtm.2023.101122. eCollection 2023 Dec 14. Mol Ther Methods Clin Dev. 2023. PMID: 37920238 Free PMC article.
Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation.
Corti M, Byrne BJ, Gessler DJ, Thompson G, Norman S, Lammers J, Coleman KE, Liberati C, Elder ME, Escolar ML, Tuna IS, Mesaros C, Kleiner GI, Barbouth DS, Gray-Edwards HL, Clement N, Cleaver BD, Gao G. Corti M, et al. Among authors: gray edwards hl. Mol Ther Methods Clin Dev. 2023 Jun 19;30:303-314. doi: 10.1016/j.omtm.2023.06.001. eCollection 2023 Sep 14. Mol Ther Methods Clin Dev. 2023. PMID: 37601414 Free PMC article.
Life-Limiting Peripheral Organ Dysfunction in Feline Sandhoff Disease Emerges after Effective CNS Gene Therapy.
Johnson AK, McCurdy VJ, Gray-Edwards HL, Maguire AS, Cochran JN, Gross AL, Skinner HE, Randle AN, Shirley JL, Brunson BL, Bradbury AM, Leroy SG, Hwang M, Rockwell HE, Cox NR, Baker HJ, Seyfried TN, Sena-Esteves M, Martin DR. Johnson AK, et al. Among authors: gray edwards hl. Ann Neurol. 2023 Nov;94(5):969-986. doi: 10.1002/ana.26756. Epub 2023 Aug 16. Ann Neurol. 2023. PMID: 37526361 Free PMC article.
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