Amelioration of metabolic and behavioral defects through base editing in the PahR408W phenylketonuria mouse model.
Yin S, Gao L, Sun X, Zhang M, Gao H, Chen X, Zhang D, Ming X, Yang L, Hu Y, Chen X, Liu M, Zhan X, Guan Y, Wang L, Han L, Zhu P, Li D.
Yin S, et al. Among authors: guan y.
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Mol Ther. 2024.
PMID: 39600089