Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency.
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J Clin Invest. 2017 May 1;127(5):1689-1699. doi: 10.1172/JCI90367. Epub 2017 Mar 27.
J Clin Invest. 2017.
PMID: 28346229
Free PMC article.
Clinical Trial.