Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A 30-Month Nonrandomized Controlled Open-Label Extension Trial.
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Mah JK, et al.
JAMA Netw Open. 2022 Jan 4;5(1):e2144178. doi: 10.1001/jamanetworkopen.2021.44178.
JAMA Netw Open. 2022.
PMID: 35076703
Free PMC article.
Clinical Trial.